Sponsors
Biogen
Biogen Inc. is an American multinational biotechnology company based in Cambridge, Massachusetts, specializing in the discovery, development, and delivery of therapies for the treatment of neurological diseases to patients worldwide.
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Ionis
Ionis is guided by world-class scientists and business leaders whose passion to innovate is matched only by their commitment to deliver transformational medicines to patients who need them.
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Ovid
Ovid Therapeutics is a biopharmaceutical company focused exclusively on developing impactful medicines for patients and families living with rare neurological disorders.
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PTC
PTC Therapeutics is a US pharmaceutical company focused on the development of orally administered small molecule drugs that regulate gene expression by targeting post-translational control mechanisms in orphan diseases.
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Roche
Roche believes it’s urgent to deliver medical solutions right now – even as they develop innovations for the future. They are passionate about transforming patients’ lives. They are courageous in both decision and action. And they believe that good business means a better world.
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Ultragenyx
Ultragenyx is a biopharmaceutical company committed to bringing to patients novel products for the treatment of rare and ultra-rare diseases, with a focus on serious, debilitating genetic diseases. Founded in 2010, the company has rapidly built a diverse portfolio of approved therapies and product candidates aimed at addressing diseases with high unmet medical need and clear biology, for which there are no approved therapies.
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Global Genes
Global Genes is a global non-profit advocacy organization for individuals and families fighting rare and genetic diseases. The organization is associated with a blue denim "Genes Ribbon" that is intended to raise awareness of patients affected by rare and genetic diseases. Global Genes uses a simple concept of "jeans and genes" to promote awareness of rare disease; its slogan is "Allies in Rare Disease".
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